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Growth charts for patients with Sanfilippo syndrome (Mucopolysaccharidosis type III)

BACKGROUND: Mucopolysaccharidosis (MPS) type III (Sanfilippo syndrome) comprises a group of rare, lysosomal storage diseases caused by the deficiency of one of four enzymes involved in the degradation of heparan sulfate. The clinical hallmark of the disease is severe neurological deterioration leadi...

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Detalhes bibliográficos
Publicado no:Orphanet J Rare Dis
Main Authors: Muschol, Nicole M., Pape, Daniel, Kossow, Kai, Ullrich, Kurt, Arash-Kaps, Laila, Hennermann, Julia B., Stücker, Ralf, Breyer, Sandra R.
Formato: Artigo
Idioma:Inglês
Publicado em: BioMed Central 2019
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6498678/
https://ncbi.nlm.nih.gov/pubmed/31046785
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-019-1065-x
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