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Variability and trends in corticosteroid use by male United States participants with Duchenne muscular dystrophy in the Duchenne Registry

BACKGROUND: Treatment options for Duchenne muscular dystrophy remain limited, although consensus treatment guidelines recommend corticosteroid use. METHODS: This retrospective analysis assessed corticosteroid use in ambulatory and nonambulatory US males with Duchenne, age 35 and under, or Becker mus...

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Publicat a:BMC Neurol
Autors principals: Cowen, Leslie, Mancini, Maria, Martin, Ann, Lucas, Ann, Donovan, Joanne M.
Format: Artigo
Idioma:Inglês
Publicat: BioMed Central 2019
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6498563/
https://ncbi.nlm.nih.gov/pubmed/31046703
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s12883-019-1304-8
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