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Reliability and validity of the instrument for scoring clinical outcomes of research for epidermolysis bullosa (iscorEB)

BACKGROUND: Epidermolysis bullosa (EB) is a group of rare and currently incurable genetic blistering disorders. As more pathogenic driven therapies are being developed, the need for EB-specific validated outcomes measures designed for use in clinical trials is becoming important. OBJECTIVES: We prev...

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Dades bibliogràfiques
Publicat a:Br J Dermatol
Autors principals: Bruckner, Anna L., Fairclough, Diane L., Feinstein, James A., Lara-Corrales, Irene, Lucky, Anne W., Tolar, Jakub, Pope, Elena
Format: Artigo
Idioma:Inglês
Publicat: 2018
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6478606/
https://ncbi.nlm.nih.gov/pubmed/29341069
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1111/bjd.16350
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