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Hematopoietic Stem Cell Transplantation in Patients with Heterozygous STAT1 Gain-of-Function Mutation

PURPOSE: Human Signal transducer and activator of transcription 1 (STAT1) gain of function (GOF) mutations present with a broad range of manifestations ranging from chronic mucocutaneous candidiasis and autoimmunity to combined immunodeficiency (CID). So far, there is very limited experience with he...

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Detalles Bibliográficos
Publicado en:J Clin Immunol
Main Authors: Kiykim, Ayca, Charbonnier, Louis Marie, Akcay, Arzu, Karakoc-Aydiner, Elif, Ozen, Ahmet, Ozturk, Gulyuz, Chatila, Talal A., Baris, Safa
Formato: Artigo
Idioma:Inglês
Publicado: 2018
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC6430975/
https://ncbi.nlm.nih.gov/pubmed/30543054
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s10875-018-0575-y
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