Chargement en cours...
Evaluating enzyme replacement therapies for Anderson-Fabry disease: commentary on a recent report
Anderson-Fabry disease (AFD) is a rare lysosomal storage disorder. Randomized controlled clinical trials (RCTs) are preferred as the highest category of evidence, but limited availability of robust evidence in rare diseases may necessitate the use of less rigorous evidence. An analysis of cohort stu...
Enregistré dans:
| Publié dans: | Genet Mol Biol |
|---|---|
| Auteurs principaux: | , , , , , |
| Format: | Artigo |
| Langue: | Inglês |
| Publié: |
Sociedade Brasileira de Genética
2018
|
| Sujets: | |
| Accès en ligne: | https://ncbi.nlm.nih.gov/pmc/articles/PMC6415596/ https://ncbi.nlm.nih.gov/pubmed/30334566 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1590/1678-4685-GMB-2017-0345 |
| Tags: |
Ajouter un tag
Pas de tags, Soyez le premier à ajouter un tag!
|