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Demyelinating Neuropathy in a Patient Treated With Revusiran for Transthyretin (Thr60Ala) Amyloidosis
Transthyretin amyloidosis patients develop length-dependent peripheral neuropathy, autonomic dysfunction, and restrictive cardiomyopathy associated with deposition of amyloid fibrils in these tissues. Despite advances in management over the past decade, this disorder causes profound debilitation and...
Gorde:
Argitaratua izan da: | J Clin Neuromuscul Dis |
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Egile Nagusiak: | , , , , |
Formatua: | Artigo |
Hizkuntza: | Inglês |
Argitaratua: |
Journal of Clinical Neuromuscular Disease
2019
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Gaiak: | |
Sarrera elektronikoa: | https://ncbi.nlm.nih.gov/pmc/articles/PMC6392216/ https://ncbi.nlm.nih.gov/pubmed/30801482 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/CND.0000000000000242 |
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