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The impact of Pompe disease on smooth muscle: a review

Pompe disease (OMIM 232300) is an autosomal recessive disorder caused by mutations in the gene encoding acid α-glucosidase (GAA) (EC 3.2.1.20), the enzyme responsible for hydrolyzing lysosomal glycogen. The primary cellular pathology is lysosomal glycogen accumulation in cardiac muscle, skeletal mus...

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Dades bibliogràfiques
Publicat a:J Smooth Muscle Res
Autors principals: MCCALL, Angela L., SALEMI, Jeffrey, BHANAP, Preeti, STRICKLAND, Laura M., ELMALLAH, Mai K.
Format: Artigo
Idioma:Inglês
Publicat: Japan Society of Smooth Muscle Research 2019
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6380904/
https://ncbi.nlm.nih.gov/pubmed/30787211
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1540/jsmr.54.100
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