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A Pilot Trial of RNS60 in Amyotrophic Lateral Sclerosis

INTRODUCTION: RNS60 is a novel immune-modulatory agent that has shown neuroprotective effects in ALS pre-clinical models. RNS60 is administered by weekly intravenous infusion and daily nebulization. The objective of this pilot open-label trial was to test the feasibility, safety, and tolerability of...

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Pubblicato in:Muscle Nerve
Autori principali: Paganoni, Sabrina, Alshikho, Mohamad J., Luppino, Sarah, Chan, James, Pothier, Lindsay, Schoenfeld, David, Andres, Patricia L., Babu, Suma, Zürcher, Nicole R., Loggia, Marco L., Barry, Robert L., Luotti, Silvia, Nardo, Giovanni, Trolese, Maria Chiara, Pantalone, Serena, Bendotti, Caterina, Bonetto, Valentina, De Marchi, Fabiola, Rosen, Bruce, Hooker, Jacob, Cudkowicz, Merit, Atassi, Nazem
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2018
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6379136/
https://ncbi.nlm.nih.gov/pubmed/30458059
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/mus.26385
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