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New Therapeutic Options for the Treatment of Sickle Cell Disease

Sickle cell disease (SCD; ORPHA232; OMIM # 603903) is a chronic and invalidating disorder distributed worldwide, with high morbidity and mortality. Given the disease complexity and the multiplicity of pathophysiological targets, development of new therapeutic options is critical, despite the positiv...

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Detalles Bibliográficos
Publicado en:Mediterr J Hematol Infect Dis
Main Authors: Matte, Alessandro, Zorzi, Francesco, Mazzi, Filippo, Federti, Enrica, Olivieri, Oliviero, De Franceschi, Lucia
Formato: Artigo
Idioma:Inglês
Publicado: Università Cattolica del Sacro Cuore 2019
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC6328043/
https://ncbi.nlm.nih.gov/pubmed/30671208
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4084/MJHID.2019.002
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