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Improvement in Cardiac Function With Enzyme Replacement Therapy in a Patient With Infantile-Onset Pompe Disease

BACKGROUND: Pompe disease is a lysosomal storage disorder that results from an inborn error of metabolism involving abnormal glycogen storage. Infantile-onset Pompe disease is the most severe phenotype, and enzyme replacement therapy with alglucosidase alfa (Lumizyme) improves medical and functional...

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Podrobná bibliografie
Vydáno v:Ochsner J
Hlavní autoři: Niyazov, Dmitriy, Lara, Diego A.
Médium: Artigo
Jazyk:Inglês
Vydáno: Academic Division of Ochsner Clinic Foundation 2018
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC6292475/
https://ncbi.nlm.nih.gov/pubmed/30559630
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.31486/toj.18.0049
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