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Allogeneic stem cell transplantation with reduced intensity conditioning for patients with adrenoleukodystrophy

OBJECTIVE: The prognosis of adrenoleukodystrophy (ALD)with neurological involvement is generally dismal; however, allogeneic stem cell transplantation (SCT) is recognized as effective to stabilize or improve the clinical symptoms of ALD. Herein, we report the clinical outcomes of patients with ALD w...

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Dades bibliogràfiques
Publicat a:Mol Genet Metab Rep
Autors principals: Kato, Koji, Maemura, Ryo, Wakamatsu, Manabu, Yamamori, Ayako, Hamada, Motoharu, Kataoka, Shinsuke, Narita, Atsushi, Miwata, Shunsuke, Sekiya, Yuko, Kawashima, Nozomu, Suzuki, Kyogo, Narita, Kotaro, Doisaki, Sayoko, Muramatsu, Hideki, Sakaguchi, Hirotoshi, Matsumoto, Kimikazu, Koike, Yuka, Onodera, Osamu, Kaga, Makiko, Shimozawa, Nobuyuki, Yoshida, Nao
Format: Artigo
Idioma:Inglês
Publicat: Elsevier 2018
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6260425/
https://ncbi.nlm.nih.gov/pubmed/30519529
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymgmr.2018.11.001
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