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Identification and Characterization of 40 Novel Hydroxymethylbilane Synthase Mutations that Cause Acute Intermittent Porphyria

Acute intermittent porphyria (AIP), an autosomal dominant disorder due to the half-normal activity of hydroxymethylbilane synthase (HMBS), is characterized by acute neurovisceral attacks that are precipitated by factors that induce heme biosynthesis. Molecular diagnosis is the most sensitive and spe...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:J Inherit Metab Dis
Egile Nagusiak: Chen, Brenden, Solis-Villa, Constanza, Erwin, Angelika L., Balwani, Manisha, Nazrenko, Irina, Phillips, John D., Desnick, Robert J., Yasuda, Makiko
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: 2019
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC6162174/
https://ncbi.nlm.nih.gov/pubmed/30740734
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jimd.12040
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