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The Clinical Cases of Geleophysic Dysplasia: One Gene, Different Phenotypes

BACKGROUND: Geleophysic dysplasia is a rare multisystem disorder that principally affects the bones, joints, heart, and skin. This condition is inherited either in an autosomal dominant pattern due to FBN1 mutations or in an autosomal recessive pattern due to ADAMTSL2 mutations. Two patients with un...

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Bibliografiset tiedot
Julkaisussa:Case Rep Endocrinol
Päätekijät: Globa, Evgenia, Zelinska, Nataliya, Dauber, Andrew
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: Hindawi 2018
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC6051107/
https://ncbi.nlm.nih.gov/pubmed/30057829
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1155/2018/8212417
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