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Elevation of plasma lysosphingomyelin-509 and urinary bile acid metabolite in Niemann-Pick disease type C-affected individuals

Niemann-Pick disease type C (NPC) is a neurovisceral disorder associated with the accumulation of lipids such as cholesterol and sphingolipids. NPC is caused by either NPC1 or NPC2, which encode lysosomal proteins located at membraneous and soluble fractions, respectively. For the past decade, the o...

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Dettagli Bibliografici
Pubblicato in:Mol Genet Metab Rep
Autori principali: Mashima, Ryuichi, Maekawa, Masamitsu, Narita, Aya, Okuyama, Torayuki, Mano, Nariyasu
Natura: Artigo
Lingua:Inglês
Pubblicazione: Elsevier 2018
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6047109/
https://ncbi.nlm.nih.gov/pubmed/30023294
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymgmr.2018.03.005
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