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Evaluator Training and Reliability for SMA Global Nusinersen Trials(1)

BACKGROUND: Training methodology was established to optimize reliability of outcome measures in the nusinersen clinical trials. The Children’s Hospital of Philadelphia Infant Test of Neuromuscular Disorders (CHOP INTEND), Hammersmith Functional Motor Scale Expanded (HFMSE), and Revised Upper Limb (R...

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Detalhes bibliográficos
Publicado no:J Neuromuscul Dis
Main Authors: Glanzman, Allan M., Mazzone, Elena S., Young, Sally Dunaway, Gee, Richard, Rose, Kristy, Mayhew, Anna, Nelson, Leslie, Yun, Chris, Alexander, Katie, Darras, Basil T., Zolkipli-Cunningham, Zarazuela, Tennekoon, Gihan, Day, John W., Finkel, Richard S., Mercuri, Eugenio, De Vivo, Darryl C., Baldwin, Ron, Bishop, Kathie M., Montes, Jacqueline
Formato: Artigo
Idioma:Inglês
Publicado em: IOS Press 2018
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6030668/
https://ncbi.nlm.nih.gov/pubmed/29865090
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3233/JND-180301
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