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Evaluator Training and Reliability for SMA Global Nusinersen Trials(1)

BACKGROUND: Training methodology was established to optimize reliability of outcome measures in the nusinersen clinical trials. The Children’s Hospital of Philadelphia Infant Test of Neuromuscular Disorders (CHOP INTEND), Hammersmith Functional Motor Scale Expanded (HFMSE), and Revised Upper Limb (R...

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Опубликовано в: :J Neuromuscul Dis
Главные авторы: Glanzman, Allan M., Mazzone, Elena S., Young, Sally Dunaway, Gee, Richard, Rose, Kristy, Mayhew, Anna, Nelson, Leslie, Yun, Chris, Alexander, Katie, Darras, Basil T., Zolkipli-Cunningham, Zarazuela, Tennekoon, Gihan, Day, John W., Finkel, Richard S., Mercuri, Eugenio, De Vivo, Darryl C., Baldwin, Ron, Bishop, Kathie M., Montes, Jacqueline
Формат: Artigo
Язык:Inglês
Опубликовано: IOS Press 2018
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC6030668/
https://ncbi.nlm.nih.gov/pubmed/29865090
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3233/JND-180301
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