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ATRT-27. A PHASE II STUDY OF PANOBINOSTAT IN PAEDIATRIC PATIENTS WITH SOLID TUMORS INCLUDING MALIGNANT RHABDOID TUMOR/ATYPICAL TERATOID RHABDOID TUMOURS

BACKGROUND: Low-dose panobinostat treatment has been shown to terminally differentiate malignant rhabdoid tumor (MRT)/atypical teratoid rhabdoid tumors (ATRT) in pre-clinical models. OBJECTIVES: This will be an open label, phase II study, of panobinostat in patients with newly diagnosed MRT/ATRT, ai...

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Detalles Bibliográficos
Publicado en:Neuro Oncol
Main Authors: Wood, Paul, Desai, Jayesh, Gottardo, Nick, Cain, Jason, Ashley, David
Formato: Artigo
Idioma:Inglês
Publicado: Oxford University Press 2018
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC6012108/
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/neuonc/noy059.025
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