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A Novel Heterozygous Intronic Mutation in the FBN1 Gene Contributes to FBN1 RNA Missplicing Events in the Marfan Syndrome

Marfan syndrome (MFS) is an autosomal dominantly inherited connective tissue disorder, mostly caused by mutations in the fibrillin-1 (FBN1) gene. We, by using targeted next-generation sequence analysis, identified a novel intronic FBN1 mutation (the c.2678-15C>A variant) in a MFS patient with aor...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Biomed Res Int
Egile Nagusiak: Torrado, Mario, Maneiro, Emilia, Trujillo-Quintero, Juan Pablo, Evangelista, Arturo, Mikhailov, Alexander T., Monserrat, Lorenzo
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: Hindawi 2018
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC5996431/
https://ncbi.nlm.nih.gov/pubmed/30003093
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1155/2018/3536495
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