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Allogeneic Hematopoietic Stem-Cell Transplantation for GATA2 Deficiency Using a Busulfan-Based Regimen

Allogeneic hematopoietic stem cell transplantation (HSCT) reverses the bone marrow failure syndrome due to GATA2 deficiency. The intensity of conditioning required to achieve reliable engraftment and prevent relapse remains unclear. Here, we describe the results of a prospective study of HSCT in 22...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Biol Blood Marrow Transplant
Egile Nagusiak: Parta, Mark, Shah, Nirali N., Baird, Kristin, Rafei, Hind, Calvo, Katherine R., Hughes, Thomas, Cole, Kristen, Kenyon, Meg, Schuver, Bazetta Blacklock, Cuellar-Rodriguez, Jennifer, Zerbe, Christa S., Holland, Steven M., Hickstein, Dennis D.
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: 2018
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC5993597/
https://ncbi.nlm.nih.gov/pubmed/29412158
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.bbmt.2018.01.030
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