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Efficient Delivery and Nuclear Uptake Is Not Sufficient to Detect Gene Editing in CD34+ Cells Directed by a Ribonucleoprotein Complex

CD34+ cells are prime targets for therapeutic strategies for gene editing, because modified progenitor cells have the capacity to differentiate through an erythropoietic lineage. Although experimental advances have been reported, the associated experimental protocols have largely been less than clea...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Mol Ther Nucleic Acids
Egile Nagusiak: Modarai, Shirin R., Man, Dula, Bialk, Pawel, Rivera-Torres, Natalia, Bloh, Kevin, Kmiec, Eric B.
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: American Society of Gene & Cell Therapy 2018
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC5992347/
https://ncbi.nlm.nih.gov/pubmed/29858048
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.omtn.2018.01.013
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