A carregar...
Development of Intrathecal AAV9 Gene Therapy for Giant Axonal Neuropathy
An NIH-sponsored phase I clinical trial is underway to test a potential treatment for giant axonal neuropathy (GAN) using viral-mediated GAN gene replacement (https://clinicaltrials.gov/ct2/show/NCT02362438). This trial marks the first instance of intrathecal (IT) adeno-associated viral (AAV) gene t...
Na minha lista:
| Publicado no: | Mol Ther Methods Clin Dev |
|---|---|
| Main Authors: | , , , |
| Formato: | Artigo |
| Idioma: | Inglês |
| Publicado em: |
American Society of Gene & Cell Therapy
2018
|
| Assuntos: | |
| Acesso em linha: | https://ncbi.nlm.nih.gov/pmc/articles/PMC5948230/ https://ncbi.nlm.nih.gov/pubmed/29766026 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.omtm.2018.02.005 |
| Tags: |
Adicionar Tag
Sem tags, seja o primeiro a adicionar uma tag!
|