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Comparison of the editing patterns and editing efficiencies of TALEN and CRISPR-Cas9 when targeting the human CCR5 gene

The human C-C chemokine receptor type-5 (CCR5) is the major transmembrane co-receptor that mediates HIV-1 entry into target CD4+ cells. Gene therapy to knock-out the CCR5 gene has shown encouraging results in providing a functional cure for HIV-1 infection. In gene therapy strategies, the initial re...

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Dettagli Bibliografici
Pubblicato in:Genet Mol Biol
Autori principali: Nerys-Junior, Arildo, Braga-Dias, Luciene P., Pezzuto, Paula, Cotta-de-Almeida, Vinícius, Tanuri, Amilcar
Natura: Artigo
Lingua:Inglês
Pubblicazione: Sociedade Brasileira de Genética 2018
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5901495/
https://ncbi.nlm.nih.gov/pubmed/29583154
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1590/1678-4685-GMB-2017-0065
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