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Slow progression of renal failure in a child with infantile cystinosis

Cystinosis is a rare autosomal recessive lysosomal transport disorder, characterized by the accumulation of the aminoacid cystine and progressive dysfunction of several organs. Kidneys are severely affected, and the most frequent form, infantile nephropathic cystinosis, presents with growth failure...

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Kaydedildi:
Detaylı Bibliyografya
Yayımlandı:CEN Case Rep
Asıl Yazarlar: Bitsori, Maria, Vergadi, Eleni, Galanakis, Emmanouil
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: Springer Japan 2018
Konular:
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC5886947/
https://ncbi.nlm.nih.gov/pubmed/29446030
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s13730-018-0316-3
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