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Infantile spasms related to a 5q31.2-q31.3 microdeletion including PURA

Recently, haploinsufficiency of PURA has been identified as an essential cause of 5q31.3 microdeletion syndrome, which is characterized by severe psychomotor developmental delay, epilepsy, distinctive features, and delayed myelination. A new 5q31.2-q31.3 microdeletion that included PURA was identifi...

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Detaylı Bibliyografya
Yayımlandı:Hum Genome Var
Asıl Yazarlar: Shimojima, Keiko, Okamoto, Nobuhiko, Ohmura, Kayo, Nagase, Hiroaki, Yamamoto, Toshiyuki
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: Nature Publishing Group 2018
Konular:
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC5874397/
https://ncbi.nlm.nih.gov/pubmed/29619234
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/hgv.2018.7
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