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Associations between timing of corticosteroid treatment initiation and clinical outcomes in Duchenne muscular dystrophy

The long-term efficacy of corticosteroid treatment and timing of treatment initiation among Duchenne muscular dystrophy (DMD) patients is not well-understood. We used data from a longitudinal, population-based DMD surveillance program to examine associations between timing of treatment initiation (e...

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Detalhes bibliográficos
Publicado no:Neuromuscul Disord
Main Authors: Kim, Sunkyung, Zhu, Yong, Romitti, Paul A., Fox, Deborah J., Sheehan, Daniel W., Valdez, Rodolfo, Matthews, Dennis, Barber, Brent J.
Formato: Artigo
Idioma:Inglês
Publicado em: 2017
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5824693/
https://ncbi.nlm.nih.gov/pubmed/28645460
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.nmd.2017.05.019
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