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Charcot Marie Tooth disease type 4J with complex central nervous system features

We describe a family with Charcot Marie Tooth disease type 4J presenting with features of Charcot Marie Tooth disease plus parkinsonism and aphemia. Genetic testing found two variants in the FIG4 gene: c.122T>C (p.I41T) – the most common Charcot Marie Tooth disease type 4J variant – and c.1949‐10...

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Dettagli Bibliografici
Pubblicato in:Ann Clin Transl Neurol
Autori principali: Orengo, James P., Khemani, Pravin, Day, John W., Li, Jun, Siskind, Carly E.
Natura: Artigo
Lingua:Inglês
Pubblicazione: John Wiley and Sons Inc. 2018
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5817837/
https://ncbi.nlm.nih.gov/pubmed/29468183
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/acn3.525
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