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SMD Kozlowski type caused by p.Arg594His substitution in TRPV4 reveals abnormal ossification and notochordal remnants in discs and vertebrae

Spondylometaphyseal dysplasia Kozlowski type (SMDK) is a monogenic disorder within the TRPV4 dysplasia spectrum and has characteristic spinal and metaphyseal involvement. We report skeletal MR imaging in a two-year-old patient who manifested typical clinical and radiographic features of SMDK. The di...

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Detalhes bibliográficos
Publicado no:Eur J Med Genet
Main Authors: Bieganski, Tadeusz, Beighton, Peter, Lukaszewski, Maciej, Bik, Krzysztof, Kuszel, Lukasz, Wasilewska, Ewa, Kozlowski, Kazimierz, Czarny-Ratajczak, Malwina
Formato: Artigo
Idioma:Inglês
Publicado em: 2017
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5785083/
https://ncbi.nlm.nih.gov/pubmed/28687525
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ejmg.2017.07.004
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