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Quality of life of Hurler syndrome patients after successful hematopoietic stem cell transplantation

Hurler syndrome (HS) is a lysosomal storage disease characterized by multisystem morbidity and death in early childhood. Hematopoietic stem cell transplantation (HSCT) results in long-term survival, although with significant residual disease burden. How this residual disease affects the health-relat...

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Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Blood Adv
Egile Nagusiak: Aldenhoven, Mieke, van den Broek, Brigitte T. A., Wynn, Robert F., O’Meara, Anne, Veys, Paul, Rovelli, Attilio, Jones, Simon A., Parini, Rossella, van Hasselt, Peter M., Renard, Marleen, Bordon, Victoria, de Koning, Tom J., Boelens, Jaap Jan
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: American Society of Hematology 2017
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC5737136/
https://ncbi.nlm.nih.gov/pubmed/29296871
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/bloodadvances.2017011387
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