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Whole-exome sequencing identifies an α-globin cluster triplication resulting in increased clinical severity of β-thalassemia

Whole-exome sequencing (WES) has been increasingly useful for the diagnosis of patients with rare causes of anemia, particularly when there is an atypical clinical presentation or targeted genotyping approaches are inconclusive. Here, we describe a 20-yr-old man with a lifelong moderate-to-severe an...

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Pubblicato in:Cold Spring Harb Mol Case Stud
Autori principali: Steinberg-Shemer, Orna, Ulirsch, Jacob C., Noy-Lotan, Sharon, Krasnov, Tanya, Attias, Dina, Dgany, Orly, Laor, Ruth, Sankaran, Vijay G., Tamary, Hannah
Natura: Artigo
Lingua:Inglês
Pubblicazione: Cold Spring Harbor Laboratory Press 2017
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5701307/
https://ncbi.nlm.nih.gov/pubmed/28667000
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1101/mcs.a001941
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