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What Is the Best Blood Sampling Time for Metabolic Control of Phenylalanine and Tyrosine Concentrations in Tyrosinemia Type 1 Patients?

Background: Treatment of hereditary tyrosinemia type 1 with nitisinone and phenylalanine and tyrosine restricted diet has largely improved outcome, but the best blood sampling time for assessment of metabolic control is not known. Aim: To study diurnal and day-to-day variation of phenylalanine and t...

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Detalhes bibliográficos
Publicado no:JIMD Rep
Main Authors: van Dam, Esther, Daly, Anne, Venema-Liefaard, Gineke, van Rijn, Margreet, Derks, Terry G. J., McKiernan, Patrick J., Rebecca Heiner-Fokkema, M., MacDonald, Anita, van Spronsen, Francjan J.
Formato: Artigo
Idioma:Inglês
Publicado em: Springer Berlin Heidelberg 2017
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5680281/
https://ncbi.nlm.nih.gov/pubmed/28120161
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2016_37
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