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Canine neuronal ceroid lipofuscinoses: Promising models for preclinical testing of therapeutic interventions

The neuronal ceroid lipofuscinoses (NCLs) are devastating inherited progressive neurodegenerative diseases, with most forms having a childhood onset of clinical signs. The NCLs are characterized by progressive cognitive and motor decline, vision loss, seizures, respiratory and swallowing impairment,...

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Detalhes bibliográficos
Publicado no:Neurobiol Dis
Main Authors: Katz, Martin L., Rustad, Eline, Robinson, Grace O., Whiting, Rebecca E.H., Student, Jeffrey T., Coates, Joan R., Narfstrom, Kristina
Formato: Artigo
Idioma:Inglês
Publicado em: 2017
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5675811/
https://ncbi.nlm.nih.gov/pubmed/28860089
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.nbd.2017.08.017
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