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Drug discovery and development for rare genetic disorders

Approximately 7,000 rare diseases affect millions of individuals in the United States. Although rare diseases taken together have an enormous impact, there is a significant gap between basic research and clinical interventions. Opportunities now exist to accelerate drug development for the treatment...

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Detalhes bibliográficos
Publicado no:Am J Med Genet A
Main Authors: Sun, Wei, Zheng, Wei, Simeonov, Anton
Formato: Artigo
Idioma:Inglês
Publicado em: 2017
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5662129/
https://ncbi.nlm.nih.gov/pubmed/28731526
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/ajmg.a.38326
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