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A Novel AGRN Mutation Leads to Congenital Myasthenic Syndrome Only Affecting Limb-girdle Muscle

BACKGROUND: Congenital myasthenic syndromes (CMSs) are a group of clinically and genetically heterogeneous disorders caused by impaired neuromuscular transmission. The defect of AGRN was one of the causes of CMS through influencing the development and maintenance of neuromuscular transmission. Howev...

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Detalhes bibliográficos
Publicado no:Chin Med J (Engl)
Main Authors: Zhang, Ying, Dai, Yi, Han, Jing-Na, Chen, Zhao-Hui, Ling, Li, Pu, Chuan-Qiang, Cui, Li-Ying, Huang, Xu-Sheng
Formato: Artigo
Idioma:Inglês
Publicado em: Medknow Publications & Media Pvt Ltd 2017
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5634075/
https://ncbi.nlm.nih.gov/pubmed/28937031
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4103/0366-6999.215332
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