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Non-derivatized Assay for the Simultaneous Detection of Amino Acids, Acylcarnitines, Succinylacetone, Creatine, and Guanidinoacetic Acid in Dried Blood Spots by Tandem Mass Spectrometry

Guanidinoacetate methyltransferase (GAMT) deficiency is an autosomal recessive genetic disorder which results in global developmental delay and intellectual disability. There is evidence that early treatment prevents intellectual disability and seizures. GAMT deficiency is now being discussed as a p...

Täydet tiedot

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Bibliografiset tiedot
Julkaisussa:Int J Neonatal Screen
Päätekijät: Asef, Carter K., Khaksarfard, Kameron M., De Jesús, Víctor R.
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: 2016
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC5580725/
https://ncbi.nlm.nih.gov/pubmed/28868498
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijns2040013
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