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Unresolved issues in hematopoietic stem cell transplantation for severe combined immunodeficiency: Need for safer conditioning and reduced late effects

In this review we discuss recent outcomes of hematopoietic cell transplantation (HCT) for patients with severe combined immunodeficiency (SCID), including survival, T- and B-cell reconstitution, and late effects, particularly those related to genotype, use of conditioning regimen, and use of alterna...

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Pubblicato in:J Allergy Clin Immunol
Autori principali: Horn, Biljana, Cowan, Morton J.
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2013
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5575916/
https://ncbi.nlm.nih.gov/pubmed/23622119
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.jaci.2013.03.014
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