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Inhaled Sargramostim Induces Resolution of Pulmonary Alveolar Proteinosis in Lysinuric Protein Intolerance

Pulmonary alveolar proteinosis (PAP) is a potentially fatal complication of lysinuric protein intolerance (LPI), an inherited disorder of cationic amino acid transport. The patients often present with mild respiratory symptoms, which may rapidly progress to acute respiratory failure responding poorl...

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Detaylı Bibliyografya
Yayımlandı:JIMD Rep
Asıl Yazarlar: Tanner, Laura M., Kurko, Johanna, Tringham, Maaria, Aho, Heikki, Mykkänen, Juha, Näntö-Salonen, Kirsti, Niinikoski, Harri, Lukkarinen, Heikki
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: Springer Berlin Heidelberg 2016
Konular:
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC5509541/
https://ncbi.nlm.nih.gov/pubmed/27783330
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2016_15
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