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Integrative Systems Biology Investigation of Fabry Disease

Fabry disease (FD) is a rare X-linked recessive genetic disorder caused by a deficient activity of the lysosomal enzyme alpha-galactosidase A (GLA) and is characterised by intra-lysosomal accumulation of globotriaosylceramide (Gb3). We performed a meta-analysis of peer-reviewed publications includin...

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Shranjeno v:
Bibliografske podrobnosti
izdano v:Diseases
Main Authors: Fernandes, Marco, Husi, Holger
Format: Artigo
Jezik:Inglês
Izdano: MDPI 2016
Teme:
Online dostop:https://ncbi.nlm.nih.gov/pmc/articles/PMC5456327/
https://ncbi.nlm.nih.gov/pubmed/28933415
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/diseases4040035
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