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Diagnosis of Morquio-A patients in Mexico: How far are we from prompt diagnosis?

Mucopolysaccharidosis IV A, better known as Morquio-A syndrome, is a rare condition with severe skeletal and multiorgan involvement. Sometimes is not easy to differentiate from other skeletal dysplasias. Prior to definitive diagnosis, patients have been delayed or misdiagnosis due to lack of knowled...

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Détails bibliographiques
Publié dans:Intractable Rare Dis Res
Auteurs principaux: Colmenares-Bonilla, Douglas, Esquitin-Garduño, Nayeli
Format: Artigo
Langue:Inglês
Publié: International Research and Cooperation Association for Bio & Socio-Sciences Advancement 2017
Sujets:
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC5451743/
https://ncbi.nlm.nih.gov/pubmed/28580212
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.5582/irdr.2017.01016
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