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FDA-Approved Oligonucleotide Therapies in 2017

Oligonucleotides (oligos) have been under clinical development for approximately the past 30 years, beginning with antisense oligonucleotides (ASOs) and apatmers and followed about 15 years ago by siRNAs. During that lengthy period of time, numerous clinical trials have been performed and thousands...

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Опубликовано в: :Mol Ther
Главные авторы: Stein, Cy A., Castanotto, Daniela
Формат: Artigo
Язык:Inglês
Опубликовано: American Society of Gene & Cell Therapy 2017
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC5417833/
https://ncbi.nlm.nih.gov/pubmed/28366767
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymthe.2017.03.023
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