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Dose-adapted post-transplant cyclophosphamide for HLA-haploidentical transplantation in Fanconi anemia

We developed a haploidentical transplantation protocol with post-transplant cyclophosphamide (CY) for in vivo T-cell depletion using a novel adapted-dosing schedule (25 mg/kg on days +3 and +4) for Fanconi Anemia. With median follow-up of 3 years (range, 37 days to 6.2 years), all six patients engra...

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Bibliografske podrobnosti
izdano v:Bone Marrow Transplant
Main Authors: Thakar, Monica S., Bonfim, Carmem, Walters, Mark C., Storb, Rainer, Pasquini, Ricardo, Burroughs, Lauri, Sandmaier, Brenda M., Woolfrey, Ann, Kiem, Hans-Peter
Format: Artigo
Jezik:Inglês
Izdano: 2017
Teme:
Online dostop:https://ncbi.nlm.nih.gov/pmc/articles/PMC5382060/
https://ncbi.nlm.nih.gov/pubmed/28067886
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/bmt.2016.301
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