Present Molecular Limitations of ON-Bipolar Cell Targeted Gene Therapy
Recent studies have demonstrated the safety and efficacy of ocular gene therapy based on adeno-associated viral vectors (AAVs). Accordingly, a surge in promising new gene therapies is entering clinical trials, including the first optogenetic therapy for vision restoration. To date, optogenetic thera...
Gorde:
Argitaratua izan da: | Front Neurosci |
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Egile Nagusiak: | , , , , |
Formatua: | Artigo |
Hizkuntza: | Inglês |
Argitaratua: |
Frontiers Media S.A.
2017
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Gaiak: | |
Sarrera elektronikoa: | https://ncbi.nlm.nih.gov/pmc/articles/PMC5372788/ https://ncbi.nlm.nih.gov/pubmed/28424574 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fnins.2017.00161 |
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