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Whole-exome sequencing and digital PCR identified a novel compound heterozygous mutation in the NPHP1 gene in a case of Joubert syndrome and related disorders

BACKGROUND: Joubert syndrome and related disorders (JSRD) is a clinically and genetically heterogeneous condition with autosomal recessive or X-linked inheritance, which share a distinctive neuroradiological hallmark, the so-called molar tooth sign. JSRD is classified into six clinical subtypes base...

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Vydáno v:BMC Med Genet
Hlavní autoři: Koyama, Shingo, Sato, Hidenori, Wada, Manabu, Kawanami, Toru, Emi, Mitsuru, Kato, Takeo
Médium: Artigo
Jazyk:Inglês
Vydáno: BioMed Central 2017
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC5368915/
https://ncbi.nlm.nih.gov/pubmed/28347285
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s12881-017-0399-2
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