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The Effect of S-Adenosylmethionine on Self-Mutilation in a Patient with Lesch–Nyhan Disease

Background: Lesch–Nyhan disease (LND) is an X-chromosomal disorder of purine metabolism characterized by hyperuricemia, dystonia, and self-mutilation, leading to an extremely high burden of disease in affected patients and families. Although allopurinol therapy can control hyperuricemia, it has no e...

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Publicado en:JIMD Rep
Autores principales: Lauber, Matthias, Plecko, Barbara, Pfiffner, Miriam, Nuoffer, Jean-Marc, Häberle, Johannes
Formato: Artigo
Lenguaje:Inglês
Publicado: Springer Berlin Heidelberg 2016
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC5362561/
https://ncbi.nlm.nih.gov/pubmed/27295197
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2016_571
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