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mTOR inhibitors in the pharmacologic management of tuberous sclerosis complex and their potential role in other rare neurodevelopmental disorders

Tuberous sclerosis complex (TSC) is a rare autosomal dominant genetic disorder that affects multiple organ systems throughout the body. Dysregulation of the mammalian target of rapamycin (mTOR) pathway is implicated in the disease pathology, and evidence exists to support the use of mTOR inhibitors...

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Détails bibliographiques
Publié dans:Orphanet J Rare Dis
Auteurs principaux: Franz, David N., Capal, Jamie K.
Format: Artigo
Langue:Inglês
Publié: BioMed Central 2017
Sujets:
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC5348752/
https://ncbi.nlm.nih.gov/pubmed/28288694
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-017-0596-2
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