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Treosulfan-Based Conditioning Regimen in Sibling and Alternative Donor Hematopoietic Stem Cell Transplantation for Children with Sickle Cell Disease

BACKGROUND AND OBJECTIVES: Lack of suitable donors and regimen related toxicity are major barriers for hematopoietic stem cell transplantation (HSCT) in patients with sickle cell disease (SCD). The aim of the study is the assessment of efficacy and toxicity of Treosulfan-based conditioning regimen f...

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Detalhes bibliográficos
Publicado no:Mediterr J Hematol Infect Dis
Main Authors: Marzollo, Antonio, Calore, Elisabetta, Tumino, Manuela, Pillon, Marta, Gazzola, Maria Vittoria, Destro, Roberta, Colombatti, Raffaella, Marson, Piero, Tison, Tiziana, Colpo, Anna, Mainardi, Chiara, Gabelli, Maria, Boaro, Maria Paola, Rossin, Sara, Strano, Aurora, Quaglia, Nadia, Menzato, Federica, Basso, Giuseppe, Sainati, Laura, Messina, Chiara
Formato: Artigo
Idioma:Inglês
Publicado em: Università Cattolica del Sacro Cuore 2017
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5333731/
https://ncbi.nlm.nih.gov/pubmed/28293402
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4084/MJHID.2017.014
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