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Treosulfan-Based Conditioning Regimen in Sibling and Alternative Donor Hematopoietic Stem Cell Transplantation for Children with Sickle Cell Disease

BACKGROUND AND OBJECTIVES: Lack of suitable donors and regimen related toxicity are major barriers for hematopoietic stem cell transplantation (HSCT) in patients with sickle cell disease (SCD). The aim of the study is the assessment of efficacy and toxicity of Treosulfan-based conditioning regimen f...

Πλήρης περιγραφή

Αποθηκεύτηκε σε:
Λεπτομέρειες βιβλιογραφικής εγγραφής
Τόπος έκδοσης:Mediterr J Hematol Infect Dis
Κύριοι συγγραφείς: Marzollo, Antonio, Calore, Elisabetta, Tumino, Manuela, Pillon, Marta, Gazzola, Maria Vittoria, Destro, Roberta, Colombatti, Raffaella, Marson, Piero, Tison, Tiziana, Colpo, Anna, Mainardi, Chiara, Gabelli, Maria, Boaro, Maria Paola, Rossin, Sara, Strano, Aurora, Quaglia, Nadia, Menzato, Federica, Basso, Giuseppe, Sainati, Laura, Messina, Chiara
Μορφή: Artigo
Γλώσσα:Inglês
Έκδοση: Università Cattolica del Sacro Cuore 2017
Θέματα:
Διαθέσιμο Online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5333731/
https://ncbi.nlm.nih.gov/pubmed/28293402
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4084/MJHID.2017.014
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