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Genome editing for inborn errors of metabolism: advancing towards the clinic

Inborn errors of metabolism (IEM) include many disorders for which current treatments aim to ameliorate disease manifestations, but are not curative. Advances in the field of genome editing have recently resulted in the in vivo correction of murine models of IEM. Site-specific endonucleases, such as...

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Detalhes bibliográficos
Publicado no:BMC Med
Main Authors: Schneller, Jessica L., Lee, Ciaran M., Bao, Gang, Venditti, Charles P.
Formato: Artigo
Idioma:Inglês
Publicado em: BioMed Central 2017
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5327528/
https://ncbi.nlm.nih.gov/pubmed/28238287
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s12916-017-0798-4
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