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A synonymous splicing mutation in the SF3B4 gene segregates in a family with highly variable Nager syndrome

Nager syndrome is a rare preaxial acrofacial dysostosis that is caused by heterozygous loss-of-function variants in SF3B4. This gene encodes for a protein required for the assembly of spliceosomal complexes, being a master gene for splicing regulation. The main clinical features of Nager syndrome in...

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Publicat a:Eur J Hum Genet
Autors principals: Cassina, Matteo, Cerqua, Cristina, Rossi, Silvia, Salviati, Leonardo, Martini, Alessandro, Clementi, Maurizio, Trevisson, Eva
Format: Artigo
Idioma:Inglês
Publicat: Nature Publishing Group 2017
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5315512/
https://ncbi.nlm.nih.gov/pubmed/27966544
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/ejhg.2016.176
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