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A Rasch Analysis of the Charcot-Marie-Tooth Neuropathy Score (CMTNS) in a Cohort of Charcot-Marie-Tooth Type 1A Patients

The Charcot-Marie-Tooth Neuropathy Score (CMTNS) was developed as a main efficacy endpoint for application in clinical trials of Charcot-Marie-Tooth disease type 1A (CMT1A). However, the sensitivity of the CMTNS for measuring disease severity and progression in CMT1A patients has been questioned. He...

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Dades bibliogràfiques
Publicat a:PLoS One
Autors principals: Wang, Wenjia, Guedj, Mickaël, Bertrand, Viviane, Foucquier, Julie, Jouve, Elisabeth, Commenges, Daniel, Proust-Lima, Cécile, Murphy, Niall P., Blin, Olivier, Magy, Laurent, Cohen, Daniel, Attarian, Shahram
Format: Artigo
Idioma:Inglês
Publicat: Public Library of Science 2017
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5240958/
https://ncbi.nlm.nih.gov/pubmed/28095456
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1371/journal.pone.0169878
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