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Genomic removal of a therapeutic mini-dystrophin gene from adult mice elicits a Duchenne muscular dystrophy-like phenotype

Duchenne muscular dystrophy (DMD) is caused by dystrophin deficiency. A fundamental question in DMD pathogenesis and dystrophin gene therapy is whether muscle health depends on continuous dystrophin expression throughout the life. Published data suggest that transient dystrophin expression in early...

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Detalhes bibliográficos
Publicado no:Hum Mol Genet
Main Authors: Wasala, Nalinda B., Lai, Yi, Shin, Jin-Hong, Zhao, Junling, Yue, Yongping, Duan, Dongsheng
Formato: Artigo
Idioma:Inglês
Publicado em: Oxford University Press 2016
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5181634/
https://ncbi.nlm.nih.gov/pubmed/27106099
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddw123
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