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Genomic removal of a therapeutic mini-dystrophin gene from adult mice elicits a Duchenne muscular dystrophy-like phenotype

Duchenne muscular dystrophy (DMD) is caused by dystrophin deficiency. A fundamental question in DMD pathogenesis and dystrophin gene therapy is whether muscle health depends on continuous dystrophin expression throughout the life. Published data suggest that transient dystrophin expression in early...

Täydet tiedot

Tallennettuna:
Bibliografiset tiedot
Julkaisussa:Hum Mol Genet
Päätekijät: Wasala, Nalinda B., Lai, Yi, Shin, Jin-Hong, Zhao, Junling, Yue, Yongping, Duan, Dongsheng
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: Oxford University Press 2016
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC5181634/
https://ncbi.nlm.nih.gov/pubmed/27106099
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddw123
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