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First case report of inherited Rubinstein-Taybi syndrome associated with a novel EP300 variant

BACKGROUND: Rubinstein-Taybi syndrome (RSTS; OMIM #180849, #613684) is a rare autosomal dominant genetic condition characterized by broad thumbs and halluces, facial dysmorphism, short stature and variable degree of intellectual disability. RSTS is associated with mutations in CREBBP and EP300 genes...

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Detalhes bibliográficos
Publicado no:BMC Med Genet
Main Authors: López, María, Seidel, Verónica, Santibáñez, Paula, Cervera-Acedo, Cristina, Castro-de Castro, Pedro, Domínguez-Garrido, Elena
Formato: Artigo
Idioma:Inglês
Publicado em: BioMed Central 2016
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5154174/
https://ncbi.nlm.nih.gov/pubmed/27964710
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s12881-016-0361-8
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