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Enzyme replacement therapy in a feline model of Maroteaux-Lamy syndrome.

We report studies that suggest enzyme replacement therapy will result in a significant reduction in disease progression and tissue pathology in patients with Maroteaux-Lamy syndrome (Mucopolysaccharidosis type VI, MPS VI). A feline model for MPS VI was used to evaluate tissue distribution and clinic...

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Dettagli Bibliografici
Autori principali: Crawley, A C, Brooks, D A, Muller, V J, Petersen, B A, Isaac, E L, Bielicki, J, King, B M, Boulter, C D, Moore, A J, Fazzalari, N L, Anson, D S, Byers, S, Hopwood, J J
Natura: Artigo
Lingua:Inglês
Pubblicazione: 1996
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC507255/
https://ncbi.nlm.nih.gov/pubmed/8621770
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